Rare diseases
Breaking News: Sarepta Therapeutics Suspends Duchenne Gene Therapy Shipments—What This Means for Patients
Sarepta Therapeutics announced it will stop shipments of Elevidys, a gene therapy for Duchenne muscular dystrophy, following a request from ... Read more
Sarepta Therapeutics Cuts One-Third of Workforce: What This Means for the Future of the Company
Sarepta Therapeutics has recently made significant cutbacks, laying off about 500 employees, which is more than one-third of its workforce. ... Read more
Understanding PolG: The Rare Genetic Disorder That Tragically Cut Short a Young Prince’s Life
Prince Frederik of Luxembourg passed away at just 22 years old due to a genetic disorder called PolG disease. His ... Read more
